Speakers Eric David Chief Executive Officer of Gene Therapy BridgeBio Johny Yao Director, Pharmacology, Translational Research Voyager Nicolas Wein Principal Investigator The Research Institute at Nationwide Children's Hospital Christian Vetterman Principle Scientist BioMarin Alison Shottek Senior Project Manager, Preclinical Programs Modalis Therapeutics Sandra Raff Senior Director - Drug Safety & Pharmacovigilance Ultragenyx Pharmaceuticals Albena Patroneva Senior Vice President Clinical Development Neurogene Kathrin Meyer Principle Investigator The Research Institute at Nationwide Children's Hospital Anas Fathallah Co-Founder Lapix Therapeutics Darin Falk Chief Scientific Officer Lacerta Genevieve Laforet Vice President - Clinical Development Aspa Therapeutics Effie Albanis Senior Vice President Early Clinical & Translational Research Neurogene Mohammadsharif Tabebordbar Co-Founder & Chief Scientific Officer Kate Therapeutics Abraham Scaria Chief Scientific Officer AGTC Kali Stasi Senior Vice President Clinical Development Adverum Mansuo Shannon Chief Scientific Officer Selecta Biosciences Eva Andres-Mateos Senior Director, Translational Research Atsena Therapeutics Weidong Xiao Professor Indiana University Ronald Crystal Professor & Chairman, Department of Genetic Medicine Weill Cornell Medical College Kei Kishimoto Chief Scientific Officer Selecta Biosciences Inc. EVENT GUIDE WORKSHOP DAY