Speakers

Eric David

Chief Executive Officer of Gene Therapy

BridgeBio

Johny Yao

Director, Pharmacology, Translational Research

Voyager

Nicolas Wein

Principal Investigator

The Research Institute at Nationwide Children's Hospital

Christian Vetterman

Principle Scientist

BioMarin

Alison Shottek

Senior Project Manager, Preclinical Programs

Modalis Therapeutics

Sandra Raff

Senior Director - Drug Safety & Pharmacovigilance

Ultragenyx Pharmaceuticals

Albena Patroneva

Senior Vice President Clinical Development

Neurogene

Kathrin Meyer

Principle Investigator

The Research Institute at Nationwide Children's Hospital

Anas Fathallah

Co-Founder

Lapix Therapeutics

Darin Falk

Chief Scientific Officer

Lacerta

Genevieve Laforet

Vice President - Clinical Development

Aspa Therapeutics

Effie Albanis

Senior Vice President Early Clinical & Translational Research

Neurogene

Mohammadsharif Tabebordbar

Co-Founder & Chief Scientific Officer

Kate Therapeutics

Abraham Scaria

Chief Scientific Officer

AGTC

Kali Stasi

Senior Vice President Clinical Development

Adverum

Mansuo Shannon

Chief Scientific Officer

Selecta Biosciences

Eva Andres-Mateos

Senior Director, Translational Research

Atsena Therapeutics

Weidong Xiao

Professor

Indiana University

Ronald Crystal

Professor & Chairman, Department of Genetic Medicine

Weill Cornell Medical College

Kei Kishimoto

Chief Scientific Officer

Selecta Biosciences Inc.