Navigating Several Aspects of Preclinical Studies to Improve Translational Safety & Success of AAV Gene Therapies

Time: 10:00 am
day: Day One


• Delving into de-targeting of AAV vectors to minimize safety concerns

• Highlighting concerns relating to AAV toxicity in NHP studies and possible methods to mitigate potential toxicity during in life study

• Exploring how to optimally use animal models to detect early signs of toxicity